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Trehalose in Machado-Joseph Disease: Safety, Tolerability, and Efficacy
Roy Zaltzman
,
Zohar Elyoseph
, Nirit Lev
, Carlos R. Gordon
Research output
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Contribution to journal
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Article
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peer-review
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Dive into the research topics of 'Trehalose in Machado-Joseph Disease: Safety, Tolerability, and Efficacy'. Together they form a unique fingerprint.
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Keyphrases
Safety Efficacy
100%
Trehalose
100%
Machado-Joseph Disease
100%
Safety/tolerability
100%
Quality of Life Questionnaire
33%
Examination Scores
33%
Neurological Examination
33%
Nine-hole Peg Test
33%
Spinocerebellar Ataxia
33%
Ataxia Score
33%
World Health Organization Quality of Life-BREF
33%
Israel
16%
Jews
16%
Quality of Life
16%
Autophagy
16%
Disease Progression
16%
Tolerability
16%
Drug Adverse Events
16%
Motor Function
16%
Neurological Impairment
16%
Conceptual Phase
16%
Cerebellar Lesion
16%
Disaccharides
16%
Lesion Size
16%
Phase I Study
16%
IV Administration
16%
Well Tolerated
16%
Pharmacology, Toxicology and Pharmaceutical Science
Tolerability
100%
Trehalose
100%
Machado Joseph Disease
100%
Ataxia
33%
Spinocerebellar Degeneration
33%
Adverse Event
16%
Disease Exacerbation
16%
Disaccharide
16%
Cerebellum Injury
16%